Support for your patients with late-onset Pompe disease (LOPD)
POMBILITI™ (cipaglucosidase alfa-atga) in combination with OPFOLDA™ (miglustat) is indicated for the treatment of adult patients with late-onset Pompe disease (lysosomal acid alpha-glucosidase [GAA] deficiency) weighing ≥40 kg and who are not improving on their current enzyme replacement therapy (ERT).
If you’ve just prescribed POMBILITI + OPFOLDA, we can help streamline the next steps. Count on AMICUS ASSIST® to provide the education and support your patients may need to get the most out of their care.
Please click here for complete Important Safety Information including BOXED WARNING for severe hypersensitivity reactions, infusion-associated reactions, and risk of acute cardiorespiratory failure in susceptible patients.
Patient Education Liaisons (PELs) and Case Managers are available to assist your patients.
Where to begin
Ready to get your patient started?
This is the first step to prescribe POMBILITI + OPFOLDA for your patient.
Want more information about the process?
Discover how to get started and explore the process for completing your patient’s enrollment.
How does AMICUS ASSIST help?
Once you’ve prescribed treatment and the patient has consented, an Amicus Patient Education Liaison (PEL) and Case Manager will be assigned to your patient.
What is a Patient Education Liaison?
Dedicated PELs can offer education and support to patients by:
Dedicated Patient Education Liaisons
can offer education and support to patients by:

Educating about LOPD and POMBILITI + OPFOLDA

Educating about LOPD and
POMBILITI + OPFOLDA

Providing tips to help patients prepare for the treatment days

Providing tips to help
patients prepare for the
treatment days

Helping patients have more productive conversations with their care team

Helping patients have more
productive conversations
with their care team
PELs do not give medical advice or take the place of the patient’s health care provider.
What is a Case Manager?
Case Managers can help patients navigate treatment access and financial assistance by:

Helping navigate their insurance coverage

Helping navigate their
insurance coverage

Helping to coordinate prescription delivery

Helping to coordinate
prescription delivery

Identifying possible sources of financial assistance

Identifying possible sources
of financial assistance
How can they both help?
With the combined knowledge and expertise of a PEL and a Case Manager, AMICUS ASSIST provides a two-pronged approach to ensure that your LOPD patients have access to the information and support they need.
Financial support for your late-onset Pompe disease (LOPD) patients
We are committed to identifying possible sources of financial assistance for your patients, including:
*Co-pay assistance is only valid for patients using commercial or private insurance for their Amicus medication. It is not valid for prescriptions reimbursed in whole or in part by Medicare, Medicaid, Veterans Administration, TRICARE, Department of Defense, similar federal or state programs, or where prohibited by law. Offer is only available for adult U.S. residents who have a valid prescription for an Amicus product. In accordance with state law, infusion-related costs are not covered for individuals residing in [RI]. Co-pay assistance is subject to annual maximum limits. Additionally, patients cannot seek reimbursement from their health insurance or other patient assistance programs for their co-pay. Amicus reserves the right to rescind, revoke, or amend this offer without notice.
†The Amicus Patient Assistance Program provides free product to those who qualify. Contact AMICUS ASSIST for details.
Amicus makes no representation or guarantee concerning reimbursement or coverage for any service or item. Information provided through the AMICUS ASSIST program does not constitute medical advice and is not intended to be a substitute for a consultation with a licensed healthcare provider or applicable third-party payer(s). Amicus reserves the right to modify the program at any time without notice.




