Late-onset Pompe disease (LOPD) resources for you
The AMICUS ASSIST Pompe disease Patient Referral Form
POMBILITI™ (cipaglucosidase alfa-atga) in combination with OPFOLDA™ (miglustat) is indicated for the treatment of adult patients with late-onset Pompe disease (lysosomal acid alpha-glucosidase [GAA] deficiency) weighing ≥40 kg and who are not improving on their current enzyme replacement therapy (ERT).
Please click here for complete Important Safety Information including BOXED WARNING for severe hypersensitivity reactions, infusion-associated reactions, and risk of acute cardiorespiratory failure in susceptible patients.
